Gene therapy for cystic fibrosis is advancing fast. Explore key biotech players, clinical progress, and its potential to ...

The genetic condition cystic fibrosis had no treatments on the NHS before 2019 and a Daily Express campaign - now a miracle one-a-day pill could make it vanish.

The new approval makes the regimen an option for around 4,000 patients in the EU who have at least one non-class I CFTR mutation.

A man with cystic fibrosis who has to do a two-hour round trip to get medication to keep him alive said a shortage of the ...

Cystic Fibrosis Ireland chief executive Sarah Tecklenborg says people can now “plan for the future with greater confidence” ...

The United States Cystic Fibrosis Foundation released the first guideline on newborn screening for cystic fibrosis (CF), in order to improve timely detection of CF in infants from all racial and ...

All states should adopt updated screening protocols so more newborns with cystic fibrosis can be diagnosed in the first weeks of life, when interventions can have the greatest benefit, according to ...

Imagine a future where treating cystic fibrosis is as simple as taking a deep breath. That’s exactly what a team of pediatric physician-scientists at the Eli and Edythe Broad Center of Regenerative ...

The Lancet Respiratory Medicine published a phase 2 clinical study article on China's first DPP-1 inhibitor, HSK31858, led by ...

Vertex Pharmaceuticals (Nasdaq: VRTX) today announced that the European Commission has granted regulatory approval for a label expansion of KAFTRIO® (ivacaftor/tezacaftor/elexacaftor) in a combination ...

The United States Cystic Fibrosis Foundation released the first guideline on newborn screening for cystic fibrosis (CF), in ...

A man with cystic fibrosis who has to do a two-hour round ... "We know how frustrating and distressing medicine supply issues can be for patients, and the pharmacists and clinicians caring for ...