Gene therapy for cystic fibrosis is advancing fast. Explore key biotech players, clinical progress, and its potential to ...

Cystic fibrosis happens because of a change in a gene on chromosome 7. This gene is responsible for making a protein called the cystic fibrosis transmembrane conductance regulator (CFTR ...

This gene normally provides instructions for the synthesis of a protein called the cystic fibrosis transmembrane conductance regulator (CFTR), which controls the movement of salt and water in and out ...

The Gairdner Foundation is pleased to announce the 2025 Canada Gairdner Award laureates, recognizing some of the world's most significant biomedical and global health research and discoveries.

Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in patients. When functioning properly, this gene produces a protein that ...

Shares in Vertex have soared after the company announced that tens of thousands of cystic fibrosis (CF ... drugs are ‘correctors’ of the CFTR protein, the defective gene that causes CF.

Dr. Michael Welsh, a longtime University of Iowa physician-scientist, has been named a 2025 recipient of the prestigious ...

Vertex Pharmaceuticals (Nasdaq: VRTX) today announced that the European Commission has granted regulatory approval for a label expansion of KAFTRIO® (ivacaftor/tezacaftor/elexacaftor) in a combination ...

MONDAY, April 14, 2025 (HealthDay News) -- Current newborn screening for cystic fibrosis favors white children over those ...