Why pharma is still far from a treatment for galactosemia
With issues in therapy delivery and a barren trial landscape, short-term chances for a commercial galactosemia treatment are ...
The American Journal of Managed Care3h
5 Rare Diseases That Now Have Their First FDA-Approved Treatments
Several rare disease patient populations received their first-ever FDA-approved drug since Rare Disease Day last year, ...
Medindia13h
Nasal Spray Offers New Hope for Brain Injury Treatment
Discover how a novel nasal spray could revolutionize traumatic brain injury treatment by reducing neuroinflammation and ...
Treatment for a disease so rare, it has no name
The nameless disease is neurodegenerative, which means it has no cure, and Ireland could face a gradual decline in her ...
Neurology Advisor2d
Ocrelizumab Treatment Safe, Effective After 96 Weeks in Minority Groups With MS
Ocrelizumab treatment in Black and Hispanic patients with MS reduces NfL levels and prevents the forming of contrast-enhancing lesions and new or enlarging T2 lesions.
Impacts4d
How Neurology Center of North Orange County Supports Alzheimer’s Patients and Their Families
Understanding the Challenges of Alzheimer’s Disease Alzheimer’s disease doesn’t just impact the person diagnosed—it affects ...
Rolling Out2h
What no one tells you about sexually transmitted infections
Explore how sexually transmitted infections progress, symptoms to watch for, and prevention strategies to protect sexual ...
KPBS2d
Did a new Alzheimer's Disease drug keep this patient's brain healthier for longer?
Sue Bell became one of the first Alzheimer's patients in the U.S. to receive the drug now marketed as Leqembi. Her husband ...
WLRN2d
Did an Alzheimer's drug give Sue and Ken Bell more time? Maybe
Sue Bell became one of the first Alzheimer's patients in the U.S. to receive the drug now marketed as Leqembi. Her husband ...
Young Wolverhampton woman seeks community support for life-saving treatment in America
A young woman from Wolverhampton, Talia Sinnott, is urgently appealing for community support to fund a life-changing medical ...
Healio6d
FDA approves first treatment for rare lipid storage disease
The FDA has approved Ctexli for the treatment of cerebrotendinous xanthomatosis (CTX), a rare lipid storage disease, in ...
'It's an everyday thing': Omaha woman discovers rare disease through social media
Could a social media post really solve years of confusion? Friedrich's Ataxia is a rare disease that only affects 1-in-50,000 people. "Looking at the way this girl moved — the unsteadiness and ...